Become a strategic partner for the industrialisation and commercialisation
of this innovation through an operating licence.

OPTI-RET

Gene therapy for retinal dystrophies

Investment: 640k€

Scope: Health

Scientific field(s): Biology and Medicinal Chemistry

Institution(s): Université Paris-Saclay, CNRS, Retina France

Development: Technology to be marketed

#Neuroprotection #GeneTherapy #RetinalDegeneration

#1

Gene therapy targeting a wide range of retinal degenerative diseases

#2

Demonstrated long-lasting neuroprotective effect during maturation

#3

Mature technology with high scientific credibility

USE CASES

  • A versatile product that can be used to treat a wide range of degenerative retinal diseases.
  • The initial applications relate to degenerative photoreceptor diseases such as retinitis pigmentosa and glaucoma.

APPLICATIONS

  • A neuroprotective protein in the retina has been discovered by the project team, thanks to their years of research into the underlying mechanism of action.
  • A gene therapy product can effectively induce a neuroprotective effect.

ADVANTAGES

  • Effective neuroprotection
  • Therapeutic effect with AAVs
  • Wide range of applications in degenerative retinal diseases
  • The team’s expertise in this field